Practicing Success

Target Exam

CUET

Subject

Biology

Chapter

Biotechnology and its Applications

Question:

What is the term used for the treatment of a genetic disorder by altering genes?

 

Options:

Gene therapy

rDNA technology

Bone marrow transplantation

Enzyme replacement therapy

Correct Answer:

Gene therapy

Explanation:

The correct answer is (a) Gene therapy.

Explanation: Gene therapy is a medical approach used to treat genetic disorders by manipulating genes. It involves introducing or altering genetic material in a person's cells to correct or replace the faulty or missing gene responsible for the disorder. The ultimate goal of gene therapy is to restore normal function to the affected cells and alleviate the symptoms of the genetic disorder.

Gene therapy holds great promise for the treatment of various genetic disorders, including inherited diseases caused by single gene mutations. However, it is still a developing field, and its application in clinical practice is carefully researched and regulated to ensure safety and efficacy.

Gene therapy is a collection of methods that allows correction of a gene defect that has been diagnosed in a child/embryo. Here genes are inserted into a person’s cells and tissues to treat a disease. Correction of a genetic defect involves delivery of a normal gene into the individual or embryo to take over the function of and compensate for the non-functional gene. The first clinical gene therapy was given in 1990 to a 4-year old girl with adenosine deaminase (ADA) deficiency .